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Join the RDCRN for FDA-NIH Rare Disease Day, February 27-28, 2025
Don’t miss the in-person and virtual celebration of FDA-NIH Rare Disease Day on February 27-28, 2025.
Rare Research Report: October 2024
Each month, we share summaries of recent Rare Diseases Clinical Research Network (RDCRN) grant-funded publications.
Pompe Disease Over Time: What We’re Learning from a Natural History Study
To learn more about Pompe disease, the Lysosomal Disease Network (LDN) is conducting a natural history study, “Lysosomal Disease Network Longitudinal Study of Pompe Disease.”
